Matt’s Promise is dedicated to making a difference
in the lives of young people affected by terminal illnesses.
Our cornerstone project is to find a cure for Duchenne Muscular Dystrophy (DMD).

Matt’s Promise is dedicated to making a difference in the lives of young people affected by terminal illnesses.
Our cornerstone project is to find a cure for Duchenne Muscular Dystrophy (DMD).

Overview

One of the key ways in which Matt’s Promise stays committed to its mission of finding a cure for Duchenne Muscular Dystrophy is through select funding of promising treatments and research. Since November 2004 we have supported our sister organization, Charley’s Fund in directing over $30 million into medical research to expedite the development of treatments for Duchenne muscular dystrophy. Initially the focus was translational research – research that moves the science from the laboratory into human clinical trials. We are pleased to report that our efforts are helping to now also fund clinical research. This is a clear indication that hopeful therapies are moving through the drug development pipeline. Through innovative partnerships with biotechnology companies and clinicians, we are having a clear and measurable impact on the speed of drug development for Duchenne muscular dystrophy. For further details, please click on each therapeutic strategy.

Exon Skipping

Novel Small Molecules

Biologicals

FDA Approved Drugs

Other Programs